Gene Therapy

$1,666,666.68 has been invested into the development of gene therapy and a further £386,000 on addressing the challenges faced in delivering the treatment.

Last year the first patient dosed in UK was by Dr Michela Guglieri whose position was funded at the DMD Hub site

We are helping clinical trial sites across the UK to get ready to deliver gene therapy, funding projects to make sure gene therapy is available to all. Read more here: https://www.duchenneuk.org/our-research/